[Hiring] Global Medical Lead LC-FAOD @Ultragenyx Pharmaceutical

Role Description

Ultragenyx is seeking a strategic and visionary physician leader to join the Global Medical Affairs team focused on LC-FAOD and triheptanoin.

Reporting to the VP Global/US Medical Affairs and Strategy, the Global Medical Lead will be an adaptable leader, willing to take a “hands on” approach and comfortable working in a fast-paced intellectual environment. This leader will be adept at leveraging their inborn errors of metabolism expertise to advance our mission to change the future of rare disease medicine.

Work Model: Remote: Officially documented as working full-time from home, with travel to Ultragenyx's offices or other locations on occasion as needed.

Responsibilities

• Lead the Global Medical Sub Team (GMST), ensuring regional medical affairs are involved in and inform the development of global medical strategy.
• Develop and drive the timely execution of the Global Medical Plan for LC-FAOD and triheptanoin in the pre-launch, launch, and post-launch phases.
• Serve as the strategic medical leader on the Program Core Team and key sub-teams, shaping development, commercialization, and lifecycle strategies through deep scientific and clinical expertise.
• Lead advisory boards, steering committees, and investigator meetings to gather key insights that inform program strategy and activities.
• Lead updates to the Integrated Evidence Generation Plan (IEP), ensuring alignment with HEOR and clinical development to address global/regional evidence gaps.
• Lead and successfully complete global medical affairs data generation activities, including real-world evidence (RWE), investigator-sponsored trials (ISTs), and other strategic evidence initiatives.
• Accountable as the medical affairs lead for Disease Monitoring Programs for LC-FAOD, providing strategic medical leadership on all aspects of the study and accountable for leading data generation and publication activities aligned to the IEP.
• Provide deep disease area and product expertise, ensuring accurate and consistent communication of clinical and scientific data.
• Lead global publication strategy and congress planning activities, ensuring timely, high-impact dissemination of data and other education initiatives.
• Lead training and provide strategic guidance and tools to regional medical affairs teams to ensure launch readiness and consistent scientific exchange.
• Build and maintain relationships with global key opinion leaders, societies, and advocacy groups to inform strategy and amplify scientific reach.
• Accountable for the medical assessment of the competitor environment and providing direction on strategic implications.
• Collaborate effectively across the business e.g. clinical development, HEOR, diagnostics, scientific communications and publications, regulatory, market access, commercial, training, and patient advocacy.

Qualifications

• Medical Doctor (MD, PhD strongly preferred) with Board Certification in Clinical/Biochemical Genetics.
• Proven expertise in the management of patients with inborn errors of metabolism, preferably mitochondrial disease.
• Recognized scientific authority with the ability to engage in advanced scientific and clinical discussions with both internal and external experts.
• Proven leadership skills including a passion for collaboration and understanding all stakeholder perspectives to drive alignment and decision-making.
• High aptitude for attention to detail, commitment to high-quality work, and a sense of passion and urgency to achieve goals and improve the lives of patients.
• Proven ability to take initiative and drive successful execution of complex projects.
• Highly analytical and strategic thinker with the ability to identify interdependencies, consider medical implications, and understand the broader goals of a program and the organization.
• Excellent communication skills, with the ability to effectively articulate scientific and strategic concepts in both written documents and verbal presentations.
• Demonstrated success leading cross functional or multidisciplinary teams, ideally in both academia and biotech.
• Willingness and ability to travel up to 15%, including domestic and international engagements.

Benefits

• Generous vacation time and public holidays observed by the company.
• Volunteer days.
• Long term incentive and Employee stock purchase plans or equivalent offerings.
• Employee wellbeing benefits.
• Fitness reimbursement.
• Tuition sponsoring.
• Professional development plans.